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Rare diseases

What is an orphan drug?

The need for these rare disease therapies is strong, and access to them can be lifesaving. Here’s how Johnson & Johnson is innovating to help give patients options.

3 health advocates; 1 Johnson & Johnson program that offers empowerment and connection

In the quest to solve the toughest health challenges, innovating therapies and finding treatments are essential—but so is supporting the patients living with these diseases. That’s exactly why Johnson & Johnson launched HealtheVoices a decade ago.

What it’s like when your baby has a rare blood disorder

A condition called fetal and neonatal alloimmune thrombocytopenia (FNAIT) can be deadly in newborns. That’s why Johnson & Johnson is passionate about developing a treatment for the disorder.

5 things we now know about myasthenia gravis

For Myasthenia Gravis Awareness Month, discover more about the disease, learn how one woman lives with this rare autoantibody condition and why Johnson & Johnson is working to find new treatments for patients like her.

What is a rare disease?

It’s estimated that over 300 million people around the globe are living with a rare disease. For Rare Disease Day, here’s what to know.

“My job is to educate about the need for new treatments for rare diseases”

Hetal Patel, an immunodermatology medical director at Johnson & Johnson, forged her own career path—and now she’s living into her passion for advocacy, education and innovation.

The quest to make neurodegenerative disease a thing of the past

Imagine reversing the course of conditions like Alzheimer’s or multiple sclerosis, in which cells of the central nervous system stop working or die. Researchers at Johnson & Johnson are hot on the trail of innovative solutions that may do just that, preventing often-debilitating symptoms along the way.

4 things we now know about the rare disease AL amyloidosis

Imagine having a disease that many doctors have never seen before. That’s what Marty Verel experienced when he was told he had AL amyloidosis—and it’s what hematologist Brendan Weiss, M.D., is determined to help change. For Rare Disease Day, Dr. Weiss shares what he’s learned studying the rare disease.

“I have a very rare illness": The unique way patients and scientists are fighting Castleman disease

Meet two men who have the rare immune system disorder: a doctor who created a groundbreaking registry for it—and a patient who signed up for it.